Clinical Trials
Clinical research is medical research that involves people like you. By taking part in clinical research, you help doctors and researchers learn more about disease and improve health care for people in the future.
Several new treatments for MPS are currently being investigated in clinical trials.
What Are Clinical Trials?
For any type of new medicine to be approved, it first must be proven to be safe and effective. The federal regulators review scientific data gathered when testing a therapy to help decide if the potential benefits of a medicine outweigh the possible risks. These data are accumulated in preclinical and clinical trials. While preclinical research involves testing the treatment of animals, clinical trials evaluate the safety and effectiveness of the treatment in people.
Typically, clinical trials are classified into four progressive phases in the development of a therapy. Find out more at Abeona Therapeutics which has an excellent resource on the four phases of clinical trials .
Why Would I Want To Take Part In a Clinical Trial?
Participating in a clinical trial can advance medical research and help being new treatments and cures to patients faster.
Results from clinical trials provide information about the benefits and risks of a potential treatment, or ways to prevent, manage or detect a disease.
The decision to volunteer for a clinical trial is important and should always be made in consultation with a physician and members of the research team.
Where Can I Find Clinical Trials for MPS Syndromes?
Register with VIPeR
If you would like to stay informed about new clinical trials and research on rare diseases including MPS sign up to the Viper registry.
Clinical Trials.gov
Check clinicaltrials.gov for the most up to date information on clinical trials that are currently recruiting participants for various MPS types. (Tip: Apply a filter for recruitment status: Recruiting or Enrolling by Invitation.)
CentreWatch
CentreWatch is a user friendly resource which uses clinicaltrials.gov as a source to list clinical trials available