Saving Ryan is the inspiring story by physician-scientist Dr. Emil Kakkis about his journey to develop a new, first-ever treatment for MPS.
Hear about the great challenges getting grant and industry support for this rare disease despite the solid science behind doing the treatment, while across the country, Mark Dant was in a quest to save his 9-year-old son, Ryan, afflicted by MPS for which there was no cure.
Through extraordinary persistence, and with a clock-ticking on Ryan’s declining health, Mr. Dant eventually learns of Dr. Kakkis and his work, whose enzyme replacement therapy could potentially treat Ryan successfully.
Listen to the story of a passionate doctor racing to bring treatment to patients like Ryan, altering the course of those living with MPS I, and saving lives – an Our Voices podcast, produced by the National MPS Society, USA.